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First ever therapy for deadly type of muscular dystrophy

Por: WPLG Local 10 Health November 07, 2023

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CORAL GABLES, Fla. – There’s new hope for children born with a fatal form of muscular dystrophy.Nicklaus Children’s Hospital is one of the first in the nation and one of only three hospitals in Florida offering Elevidys, an FDA approved infusion medication for the treatment of Duchenne Muscular Dystrophy.“So the goal is that you stop the disease progression so that the patients can maintain the muscle function they have up and until that... + full article



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