Nation
World
Politics
Sports
Business
Entertainment
Life
Tech
Science
Opinion
Crime
Health
Oddities

First gene therapy for deadly form of muscular dystrophy gets FDA approval for young kids

Por: WPLG Local 10 Health June 23, 2023

thumbnail

WASHINGTON – The first gene therapy for a deadly form of muscular dystrophy received preliminary U.S. approval on Thursday despite concerns from some government scientists about the treatment's ability to help boys with the inherited disease.The Food and Drug Administration approval provides a new option for some patients with Duchenne muscular dystrophy, a rare muscle-wasting disease that causes weakness, loss of mobility and early... + full article



Similar News

First gene therapy for deadly form of muscular dystrophy gets FDA approval for young kids

ABC News USA Health June 23, 2023

thumbnailWASHINGTON -- The first gene therapy for a deadly form of muscular dystrophy received preliminary U.S. approval on Thursday despite concerns from some government scientists about the treatment's ability to help boys with the inherited disease.The Food and Drug... + más

Bills' Nyheim Hines opens up about family members' struggles with muscular dystrophy, hopes to inspire people | Fox News

First gene therapy for deadly form of muscular dystrophy gets FDA approval for young kids | WPLG Local 10


Cambridge biotech Sarepta wins fast-track approval for the first muscular dystrophy gene therapy

The Boston Globe USA Business June 22, 2023

thumbnailThe Food and Drug Administration on Thursday approved the first gene therapy for Duchenne muscular dystrophy, a $3.2 million one-time treatment from a Cambridge biotech for a deadly inherited neuromuscular disorder that afflicts more than 10,000 boys and young men in the US.But... + más

FDA advisers recommend accelerated approval of a Sarepta gene therapy | The Boston Globe

First gene therapy for deadly form of muscular dystrophy gets FDA approval for young kids | ABC News


High school scores and top performers from Tuesday, March 28

Orlando Sentinel USA Sports March 29, 2023

thumbnailLake Brantley 9, Seminole 6 (8 inn.) Buzz: Jackson Golden went 2-for-5 with 2 home runs and 6 RBI for Lake Brantley. Ben Colley had a home run. Bryce Carter had 2 hits for Seminole. Mount Dora Christian Academy 10, Oak Hall (Gainesville) 4 Buzz: Collin Priest went 5-for-5 with a... + más

NFL Playoff Scenarios | ABC News

Le Krewe du Roi celebrates the state at 58th annual Mardi Gras Ball | The Advocate


High school scores and top performers from Friday, March 24

Orlando Sentinel USA Sports March 25, 2023

thumbnailOrangewood Christian 11, The Master’s Academy 1 Buzz: Austin Waring threw 5 innings of 1-run ball (0 earned runs) while allowing 4 hits and striking out 8 for Orangewood Christian. He lowered his season ERA to 0.78. Aiden McKee went 3-for-3 with a double, a walk, an RBI and a... + más

NFL Playoff Scenarios | ABC News

Le Krewe du Roi celebrates the state at 58th annual Mardi Gras Ball | The Advocate


High school scores and top performers from Tuesday, March 7

Orlando Sentinel USA Sports March 08, 2023

thumbnailThe Master’s Academy 12, Lake Highland Prep 0 Buzz: Jackson Bellhorn pitched a complete game with 8 strikeouts for Master’s. Colby Cason went 1-for-2 with 2 RBI, Trey Seluk went 1-for-3 with a double and 2 RBI. Joey Talbot pitched 3 innings striking out 4 for the... + más

NFL Playoff Scenarios | ABC News

Le Krewe du Roi celebrates the state at 58th annual Mardi Gras Ball | The Advocate


Bills' Nyheim Hines opens up about family members' struggles with muscular dystrophy, hopes to inspire people

Fox News USA Sports February 16, 2023

thumbnailNyheim Hines had a challenging 2022 season as he was traded from the Colts to the after he spent the first four full seasons of his NFL career in Indianapolis. But for the veteran running back, life on the field can pale in comparison to what’s happening off it.Hines recently... + más

Bills' Nyheim Hines believes NFL will listen to players about field conditions, shares insight on Josh Allen | Fox News

AFC-best Bills trade Zack Moss, pick to Colts for RB Nyheim Hines | ABC News


First participant in test of custom gene editing therapy dies

The Boston Globe USA Business November 05, 2022

thumbnailA man with muscular dystrophy who was first in line to receive an experimental gene editing therapy tailor-made to treat the cause of his rare form of the disease has died.The creation of for Terry Horgan, 27, was helmed by the Boston- and Connecticut-based nonprofit Cure Rare... + más

Boston startup Ascidian Therapeutics charts vision for therapies that ‘rewrite RNA’ | The Boston Globe

Death in CRISPR gene therapy study sparks search for answers | ABC News



About iurex | Privacy Policy | Disclaimer |