Por: RTTNews Health December 15, 2023
Vertex Pharmaceuticals Inc. () announced Friday that the European Medicines Agency's (EMA's) Committee for Medicinal Products for Human Use (CHMP) has adopted a positive opinion for the conditional approval of CASGEVY (exagamglogene autotemcel [exa-cel]), a CRISPR/Cas9 gene-edited therapy, for the treatment of severe sickle cell disease (SCD) and transfusion-dependent beta thalassemia (TDT).If approved, exa-cel would be the only... + full article
The New York Times USA Health December 09, 2023
On Friday, the Food and Drug Administration approved the first gene editing therapy ever to be used in humans, for sickle cell disease, a debilitating blood disorder caused by a single mutated gene.The agency also approved a second treatment using conventional gene therapy for... + más
FDA considers 1st CRISPR gene editing treatment that may cure sickle cell disease | ABC7
FDA approves 2 gene therapies for sickle cell. One is the first to use the editing tool CRISPR | WPLG Local 10
WPLG Local 10 USA Health December 09, 2023
Regulators on Friday approved two gene therapies for sickle cell disease that doctors hope can cure the painful, inherited blood disorder that afflicts mostly Black people in the U.S.The Food and Drug Administration said the one-time treatments can be used for patients 12 and... + más
What Are the Duties of A Trustee? | Forbes
Two gene therapies for sickle cell disease approved in U.S. | Los Angeles Times
RTTNews USA Health November 30, 2023
The month of November witnessed a couple of notable firsts, including the approval of the first treatment for congenital thrombotic thrombocytopenic purpura, the first chikungunya vaccine and the first treatment for progressing desmoid tumors.So far, this year, the FDA has... + más
Daydream Believers: Read This Before You Invest In AI | Forbes
US health system will go 'bankrupt' in 'a few years,' biotech entrepreneur warns | Fox Business
CBS News USA Health November 16, 2023
Expert joins CBS New York to discuss new sickle cell treatment Britain's medicines regulator has authorized the world's first treatment for , in a move that could offer relief to thousands of people with the crippling disease in the U.K.In a statement on Thursday, the... + más
UK becomes 1st country to approve gene therapy treatment for sickle cell, thalassemia | WPLG Local 10
Britain becomes 1st country to approve gene-therapy treatment for sickle cell disease | Los Angeles Times
WPLG Local 10 USA Politics November 16, 2023
LONDON – Britain's medicines regulator has authorized the world's first gene therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling disease in the U.K.In a statement on Thursday, the Medicines and... + más
Study: Too few kids with sickle cell get stroke screen, care | Associated Press
Los Angeles Times USA Science November 16, 2023
Britain's medicines regulator has authorized the world's first gene-therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling disease in the U.K. In a statement on Thursday, the Medicines and Healthcare... + más
Forbes USA Business March 27, 2023
Light Bulbs Concept Shining ETHICS, RESPECT, HONESTY and INTEGRITYgetty Previously, I wrote on in some detail, but did not go into the duties the Trustee of a Trust owes to the Trust’s beneficiary. To summarize, a Trust is an agreement written by the owner of the property,... + más
Selecting The Right Trustee To Manage Your Trust | Forbes
Author Post: Using Land Trusts For Anonymity And Asset Protection | Forbes
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