Por: Los Angeles Times Science December 08, 2023
Regulators on Friday approved two new gene therapies for sickle cell disease that doctors hope can cure the painful, inherited blood disorder that afflicts mostly Black people in the U.S. The Food and Drug Administration said the one-time treatments can be used for patients 12 and older with severe forms of the disease. One, made by Vertex Pharmaceuticals and CRISPR Therapeutics, is the first approved therapy based on CRISPR, the gene editing... + full article
New York Post USA Life December 11, 2023
For the first time in history, there’s hope that the debilitating illness known as sickle cell disease may be treatable — even cured. The Food and Drug Administration announced Friday that two gene therapies for sickle cell disease have been approved following years of... + más
Study: Too few kids with sickle cell get stroke screen, care | Associated Press
FDA considers 1st CRISPR gene editing treatment that may cure sickle cell disease | ABC7
WPLG Local 10 USA Health December 09, 2023
Regulators on Friday approved two gene therapies for sickle cell disease that doctors hope can cure the painful, inherited blood disorder that afflicts mostly Black people in the U.S.The Food and Drug Administration said the one-time treatments can be used for patients 12 and... + más
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Two gene therapies for sickle cell disease approved in U.S. | Los Angeles Times
Ars Technica USA Science December 09, 2023
Navigate Filter by topic Settings Front page layout Site theme - Dec 8, 2023 11:27 pm UTC / This digitally colorized scanning electron micrograph (SEM) revealed some of the comparative ultrastructural morphology between normal red blood cells (RBCs), and a sickle cell RBC (left)... + más
Portland Press Herald USA World December 08, 2023
In a major advance, the Food and Drug Administration on Friday approved two gene therapies that target sickle cell disease, one of which is the first commercially available treatment in the United States based on gene editing technology. The historic move offers hope for a... + más
FDA approves 2 gene therapies for sickle cell. One is the first to use the editing tool CRISPR | WPLG Local 10
Los Angeles Times USA Science November 16, 2023
Britain's medicines regulator has authorized the world's first gene-therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling disease in the U.K. In a statement on Thursday, the Medicines and Healthcare... + más
ABC7 USA Health November 01, 2023
anemia that she knew. The executive director of the nonprofit patient advocacy group the Sickle Cell Consortium was diagnosed with sickle cell disease at age three. Because of it, she's had heart problems, had her hips replaced, and experienced serious pain all her... + más
Vor Biopharma says first patient given its gene editing therapy for leukemia is in remission | The Boston Globe
Associated Press USA Science September 21, 2022
FILE - This 2009 colorized microscope image made available by the Sickle Cell Foundation of Georgia via the Centers for Disease Control and Prevention shows a sickle cell, left, and normal red blood cells of a patient with sickle cell anemia. A study of U.S. children with sickle... + más
Study: Too few kids with sickle cell get stroke screen, care | ABC News
Playing with your emotions? A Boston video game startup aims to help kids regulate their behavior. | The Boston Globe
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