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Sickle-Cell Treatment Created With Gene Editing Wins U.K. Approval

Por: The New York Times Health November 17, 2023

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Regulators in Britain on Thursday the first treatment derived from CRISPR, the revolutionary gene-editing method. Called Casgevy, the treatment is intended to cure sickle-cell disease and a related condition, beta thalassemia.The manufacturers, Vertex Pharmaceuticals, based in Boston, and CRISPR Therapeutics, based in Switzerland, say about 2,000 patients in Britain with sickle-cell disease or beta thalassemia are expected to be eligible for its... + full article



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