Por: RTTNews Health September 18, 2023
Orchard Therapeutics (), a global gene therapy leader, announced Monday that the U.S. Food and Drug Administration (FDA) has accepted the filing of its Biologics License Application (BLA) for OTL-200 in metachromatic leukodystrophy (MLD) under Priority Review.The BLA for OTL-200 is based on data from 39 pediatric patients with early-onset MLD, enrolled in two prospective non-randomized clinical studies or treated under expanded access... + full article
RTTNews USA Health June 21, 2023
bluebird bio, Inc. () announced Wednesday that the U.S. Food and Drug Administration (FDA) has accepted the Biologics License Application (BLA) for lovotibeglogene autotemcel (lovo-cel) for priority review. The agency has set a Prescription Drug User Fee Act (PDUFA) goal date of... + más
Bluebird Lake Placid Debuts In The Adirondacks | Forbes
Why Bluebird Backcountry Is The Most Unique Ski Resort In The U.S. | Forbes
RTTNews USA Health May 24, 2023
Sarepta Therapeutics, Inc. () on Wednesday provided the following update on the Biologics License Application (BLA) for SRP-9001 (delandistrogene moxeparvovec), which is currently under review for the treatment of ambulant individuals with Duchenne muscular dystrophy (DMD) who... + más
FDA advisers recommend accelerated approval of a Sarepta gene therapy | The Boston Globe
Sarepta Submits BLA For SRP-9001 To Treat Ambulant Patients With Duchenne Muscular Dystrophy | RTTNews
Orlando Sentinel USA Sports March 29, 2023
Lake Brantley 9, Seminole 6 (8 inn.) Buzz: Jackson Golden went 2-for-5 with 2 home runs and 6 RBI for Lake Brantley. Ben Colley had a home run. Bryce Carter had 2 hits for Seminole. Mount Dora Christian Academy 10, Oak Hall (Gainesville) 4 Buzz: Collin Priest went 5-for-5 with a... + más
NFL Playoff Scenarios | ABC News
Le Krewe du Roi celebrates the state at 58th annual Mardi Gras Ball | The Advocate
Orlando Sentinel USA Sports March 25, 2023
Orangewood Christian 11, The Master’s Academy 1 Buzz: Austin Waring threw 5 innings of 1-run ball (0 earned runs) while allowing 4 hits and striking out 8 for Orangewood Christian. He lowered his season ERA to 0.78. Aiden McKee went 3-for-3 with a double, a walk, an RBI and a... + más
Orlando Sentinel USA Sports March 08, 2023
The Master’s Academy 12, Lake Highland Prep 0 Buzz: Jackson Bellhorn pitched a complete game with 8 strikeouts for Master’s. Colby Cason went 1-for-2 with 2 RBI, Trey Seluk went 1-for-3 with a double and 2 RBI. Joey Talbot pitched 3 innings striking out 4 for the... + más
The New York Times USA Health January 24, 2023
Suhellen Oliveira Da Silva was six months pregnant when she learned that the child she was carrying had the same disease that had left her firstborn son paralyzed and nearly mute. But this time, there was a treatment available that could make a profound difference. This baby... + más
What Are Vampire Facials And Other Vampire Therapies? A Doctor Explains | Forbes
Boston startup Ascidian Therapeutics charts vision for therapies that ‘rewrite RNA’ | The Boston Globe
RTTNews USA Health November 14, 2022
Biopharmaceutical company Protalix BioTherapeutics, Inc. () announced Monday the resubmission on Wednesday of a Biologics License Application (BLA) to the U.S. Food and Drug Administration (FDA) for PRX-102 (pegunigalsidase alfa) for the treatment of adult patients with Fabry... + más
Valtteri Bottas Is Thriving In Leadership Role With Alfa Romeo | Forbes
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