Por: 10 WBNS Health January 24, 2023
BANGKOK, Thailand — When Rylae-Ann Poulin was a year old, she didn’t crawl or babble like other kids her age. A rare genetic disorder kept her from even lifting her head. Her parents took turns holding her upright at night just so she could breathe comfortably and sleep. Then, months later. doctors delivered gene therapy directly to her brain. Now the 4-year-old is walking, running, swimming, reading and riding horses — “just doing so... + full article
Associated Press USA Health January 24, 2023
When Rylae-Ann Poulin was a year old, she didn’t crawl or babble like other kids her age. A rare genetic disorder kept her from even lifting her head. Her parents took turns holding her upright at night just so she could breathe comfortably and sleep.Then, months later.... + más
Gene therapy has made some recent progress—is it enough? | Ars Technica
Promising gene therapy delivers treatment directly to brain | 10 WBNS
Ars Technica USA Science January 05, 2023
Navigate Filter by topic Settings Front page layout Site theme - Jan 5, 2023 12:45 pm UTC MARK GARLICK/SCIENCE PHOTO LIBRARY Share this story Gene therapy has had a long and bumpy history. Although researchers have made some notable and Despite these issues, experts say there... + más
Opinion | The New York Times
First participant in test of custom gene editing therapy dies | The Boston Globe
The New York Times USA Opinion December 09, 2022
The parents of a 2-year-old girl write that their daughter “could die within the next year” because a genetic mutation is causing her heart to fail.“Time is quickly running out for me,” writes a man in his mid-30s whose DNA harbors a genetic mistake certain to destroy... + más
Justice Alito accused of being SCOTUS leaker after new report: Disgrace | Newsweek
Why would Mac Jones get a second opinion on his injury, and how common is that? | The Boston Globe
ABC News USA Health November 23, 2022
WASHINGTON -- U.S. regulators on Tuesday approved the first gene therapy for hemophilia, a $3.5 million one-time treatment for the blood-clotting disorder.The Food and Drug Administration cleared Hemgenix, an IV treatment for adults with hemophilia B, the less common form of the... + más
FDA approves most expensive drug ever, $3.5 million-per-dose gene therapy for hemophilia B | CBS News
$3.5M gene therapy for hemophilia gets FDA approval | WPLG Local 10
WPLG Local 10 USA Health November 23, 2022
WASHINGTON – U.S. health regulators on Tuesday approved the first gene therapy for hemophilia, a $3.5 million one-time treatment for the blood-clotting disorder.The Food and Drug Administration cleared Hemgenix, an IV treatment for adults with hemophilia B, the less common... + más
$3.5M gene therapy for hemophilia gets FDA approval | ABC News
CBS News USA Health November 23, 2022
Washington — U.S. health regulators on Tuesday approved the first gene therapy for hemophilia, a $3.5 million one-time treatment for the blood-clotting disorder. The Food and Drug Administration cleared Hemgenix, an IV treatment for adults with hemophilia B, the less common... + más
Associated Press USA Science November 23, 2022
WASHINGTON (AP) — U.S. health regulators on Tuesday approved the first gene therapy for hemophilia, a $3.5 million one-time treatment for the blood-clotting disorder.The Food and Drug Administration cleared Hemgenix, an IV treatment for adults with hemophilia B, the less... + más
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