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Potential cure for sickle cell disease raises few concerns for FDA panel

Por: CBS News Politics November 01, 2023

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A panel of the Food and Drug Administration's outside advisers voiced few concerns Tuesday during a daylong wrestling with any potential risks posed by a new therapy that could cure sickle cell disease using a called .If approved by the FDA, the infusion called exa-cel, from Vertex Pharmaceuticals, could be the first cure available for many patients battling severe forms of the rare and debilitating blood disorder. The FDA is due to decide... + full article



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